Search Tag: rare diseases
2019 22 May
How can healthcare accelerate the implementation of the science? Where is Personalised Medicine (PM) already improving the lives of patients and what is needed to make it the standard of care across multiple conditions? What’s your brief at the PMC? I have a science and genetics background and bring scientific...Read more
2015 27 Feb
Rare Disease Day is observed on the final day of February each year. What began as a European event has become a worldwide campaign, with thousands of events taking place in dozens of countries. This year, the theme is “Living with a Rare Disease”, which recognises the millions of family members and friends supporting patients with rare diseases. The...Read more
2015 12 Jan
The European Medical Agency (EMA) has shown its support for a record number of orphan medicines in 2014. Out of a total of 82 medicines for human use, 17 are indicated for the treatment of a rare disease. EMA has given positive opinions on 40 new non-orphan drugs, three biosimilars, one drug for paediatric use and 21 generic, hybrid and informed consent...Read more